Loading...
Dernières publications
-
Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
-
A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
-
Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Activin Receptors
Animal/physiopathology
L-Type
Genomic
Metabolism
DMD
Duchenne DMD dystrophy
Delivery
Becker muscular dystrophy
Molecular docking
Modificateurs de gènes
DHPR α1S
Centronuclear myopathy
Knockout
Muscular dystrophy
Muscle
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Immunoglobulin Fc Fragments/pharmacology
Becker muscular dystrophy BMD
Autophagy
Cachexia
Inbred mdx
Mitochondrial fission
Animals
LncRNA
LKB1
Gene Expression Regulation/drug effects
Dystrophin-EGFP
Gene expression
Myogenesis
Gene modifiers
Génomique
Diseases
NNOS
Dystrophie Musculaire de Becker BMD
Invivo
Hepatocellular carcinoma
LncARN
Hear
Energy Metabolism/drug effects
Calcium Channels
Inhibitors
Inbred C57BL
Cell Biology
Human Umbilical Vein Endothelial Cells
BMD
Dystrophy
Cardiomyopathie
Dynamin 2
CaVβs
Dystrophin central domain
Exon skipping
Morphogenesis
Cells
Multi resolution modeling
Muscle development
Long noncoding RNA
Cell Line
NAD+
Allele‐specific silencing therapy
Base Sequence
Mice
Mdx mouse
CaV subunits
Drp1
Muscular Dystrophy
Ex-vivo
Humans
Calcium
Muscles/physiopathology
Liver
CD38
Long QT
CTNNB1
Muscle Strength
MiARN
Clinical trials
Cardiomyopathy
Homeostasis
Duchenne muscular dystrophy
Dystrophie Musculaire de Duchenne DMD
Cultured
MES
Dystrophine
Molecular Sequence Data
Duchenne muscular dystrophy DMD
Muscle Biology
Dystrophin
Myotendinous junction
Becker BMD muscular dystrophy
Antisense oligonucleotides
Epigenetics
Muscular Atrophy
Skeletal muscle
Male
Cell homeostasis
DMO
Multiresolution modeling
Dystrophie musculaire de Becker
Multi exon skipping